The U.S. House of Representatives recently approved legislation to renew a key U.S. Food & Drug Administration (FDA) program that has been instrumental in developing rare disease treatments, including those for spinal muscular atrophy (SMA).The FDA's Rare Pediatric...

Decisions about SMA treatment should be made solely by individuals with SMA and their family, in consultation with their healthcare providers. Unfortunately, some health insurance plans include barriers, such as prior authorizations or step therapy (also known as step...

Many individuals with SMA and other disabilities rely on the Supplemental Security Income (SSI) Program to meet their basic living needs such as food, clothing, and shelter. In many states, individuals enrolled in SSI are also automatically eligible for Medicaid and its...

New federal research into spinal muscular atrophy (SMA) is crucial in addressing SMA-related health complications and independence barriers faced by children and adults with SMA.  Past federal research has led to SMA treatment breakthroughs and a better understanding...

Many individuals with disabilities, including those living with SMA, struggle to find accessible housing that they can afford. While there are public accessible housing programs, there is often insufficient supply of rental vouchers. Working adults with SMA and other...

For 50 years, students with spinal muscular atrophy (SMA) and other disabilities have benefited from the programs and protections established through the Individuals with Disabilities Education Act (IDEA). Cure SMA has long advocated for full funding and enforcement of...

Natural disasters such as hurricanes, fires, tornadoes, and floods are increasingly disrupting the lives and livelihoods of Americans. A short- or long-term out-of-state relocation due to a natural disaster or other emergency can create unique challenges for...